ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
ASPsiRNA ID | Mutant allele/ASP-siRNA | Efficacy for mutant(%) |
Efficacy for wild (%) |
Relative Difference (%) | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
aspsirna3441 | GUUUGAGCUAAUGUAUGUG CAAACUCGAUUACAUACAC |
60 | 8 | 52 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3442 | GUUUGAGCUGAUGUAUGUGU CAAACUCGACUACAUACACA |
70 | 20 | 50 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3451 | GUUUGAGCUAAUGUAUGUG CAAACUCGAUUACAUACAC |
60 | 8 | 52 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3452 | GUUUGAGCUGAUGUAUGUGU CAAACUCGACUACAUACACA |
70 | 20 | 50 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3461 | GUUUGAGCUAAUGUAUGUG CAAACUCGAUUACAUACAC |
60 | 8 | 52 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3462 | GUUUGAGCUGAUGUAUGUGU CAAACUCGACUACAUACACA |
70 | 20 | 50 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3471 | GUUUGAGCUAAUGUAUGUG CAAACUCGAUUACAUACAC |
60 | 8 | 52 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3472 | GUUUGAGCUGAUGUAUGUGU CAAACUCGACUACAUACACA |
70 | 20 | 50 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3481 | GUUUGAGCUAAUGUAUGUG CAAACUCGAUUACAUACAC |
60 | 8 | 52 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3482 | GUUUGAGCUGAUGUAUGUGU CAAACUCGACUACAUACACA |
70 | 20 | 50 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3491 | GUUUGAGCUAAUGUAUGUG CAAACUCGAUUACAUACAC |
60 | 0 | 60 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 | ||
aspsirna3492 | GUUUGAGCUGAUGUAUGUGU CAAACUCGACUACAUACACA |
70 | 30 | 40 | HTT | Huntington disease (HD) | NM_002111.7:c.8163G>A | rs2276881 |